Can lab grown tissues help test drugs for rare diseases?

Medscape | 
Marshall L. Summar, MD: I am Marshall Summar, Chief of Genetics and Metabolism at Children's National Medical Center in Washington, ...

Impacts of genetic analysis and patient advocacy for extremely rare diseases

Medscape | 
Marshall L. Summar, MD, Chief of the Division of Genetics and Metabolism at Children's National Medical Center in Washington, DC, ...
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