Why life-saving gene therapy isn't available yet to children who need it most

Why life-saving gene therapy isn’t available yet to children who need it most

[The first patient to permanently edit his DNA,] Brian Madeux, 44, of Arizona, is part of a clinical trial testing ...
How gene therapy could help fight methamphetamine addiction

How gene therapy could help fight methamphetamine addiction

Gene therapy, which modifies a person’s DNA, has long been thought of as a way to treat genetic diseases—and, more recently, ...
Talking Biotech: Pet dogs with genetic diseases testing ground for gene therapy

Talking Biotech: Pet dogs with genetic diseases testing ground for gene therapy

Journalist Emily Mullin: Gene therapies becoming more promising but restricted in humans because of safety concerns, prompting some researchers to ...
Inserting CRISPR machinery into human cells to fight Huntington's and Lou Gehrig's

Inserting CRISPR machinery into human cells to fight Huntington’s and Lou Gehrig’s

The gene-editing tool CRISPR is based on a natural defense system embedded in bacterial cells that recognizes and destroys invading ...
Edible ‘CRISPR pill’ could make harmful bacteria self-destruct

Edible ‘CRISPR pill’ could make harmful bacteria self-destruct

As resistance to antibiotics grows in the U.S., researchers are looking for new ways to fight germs like Clostridium difficile, a ...
$500K gene therapy treatment? Some see a bargain

$500K gene therapy treatment? Some see a bargain

The idea behind gene therapy is that genetic material is used as a “living drug” to treat disease. Scientists have been ...
5 companies leading the personal genomics revolution

5 companies leading the personal genomics revolution

As gene sequencing technology gets faster and cheaper, companies are finding more ways to commercialize DNA, from offering disease-specific genetic ...
What's next in consumer genetics? Helix's 'app store for your genome'

What’s next in consumer genetics? Helix’s ‘app store for your genome’

A Silicon Valley startup called Helix is betting on the notion that not only do people want to learn more ...
Darwin Life: 'Three-parent babies' as a cure for age-related infertility

Darwin Life: ‘Three-parent babies’ as a cure for age-related infertility

John Zhang, a U.S. fertility doctor has started a company [called Darwin Life] with a provocative vision for older women: become ...
Physicians missing cancer diagnoses by not ordering gene tests

Physicians missing cancer diagnoses by not ordering gene tests

A small company called Loxo Oncology thinks it can treat every cancer patient that harbors a specific, unusual, genetic mutation...The ...
Keytruda drug treats cancer based on tumor's genetics rather than its location

Keytruda drug treats cancer based on tumor’s genetics rather than its location

In a first for precision medicine, a cancer drug has won regulatory approval based on the genetic characteristic of tumors, ...
Bubble boy hope: Strimvelis gene therapy revises genetic make-up, offers rare immune deficiency cure

Bubble boy hope: Strimvelis gene therapy revises genetic make-up, offers rare immune deficiency cure

A child in Europe has become the second individual ever to receive a commercial gene therapy, according to GlaxoSmithKline. The ...
Edible 'CRISPR pill' instructs harmful bacteria to self-destruct, may revolutionize fight against antibiotic resistance

Edible ‘CRISPR pill’ instructs harmful bacteria to self-destruct, may revolutionize fight against antibiotic resistance

As resistance to antibiotics grows in the U.S., researchers are looking for new ways to fight germs like Clostridium difficile, ...
No longer waiting idly: Parents of patients establishing gene therapy programs

No longer waiting idly: Parents of patients establishing gene therapy programs

In recent years, gene therapies have become safer and better at hitting their intended targets in the body, leading to ...
5 biotech products US regulators might struggle to regulate

5 biotech products US regulators might struggle to regulate

A new report issued by the National Academy of Sciences says U.S. regulatory agencies need to prepare for new plants, ...
'Speeding up evolution': Artificial yeast project could boost drug, biofuel production

‘Speeding up evolution’: Artificial yeast project could boost drug, biofuel production

An international team of scientists is closing in on its goal of replacing all the genetic material in a yeast ...
Brain cancer in children: Unique 'genetic drivers' open door to precision medical treatments

Brain cancer in children: Unique ‘genetic drivers’ open door to precision medical treatments

In the past 30 years, childhood deaths from cancer have declined by 50 percent overall, but those from pediatric brain ...
Our voices and smartphones may soon help diagnose diseases and stress disorders

Our voices and smartphones may soon help diagnose diseases and stress disorders

Voice samples are a rich source of information about a person’s health, and researchers think subtle vocal cues may indicate ...

Personalized cancer vaccines could revolutionize treatment and prevent relapse

Ernest Levy joined an early-stage clinical trial led by the Beth Israel Deaconess Medical Center, testing a cancer vaccine for ...
Bug gene therapy: Helpful insects could carry genes to protect diseased crops

Bug gene therapy: Helpful insects could carry genes to protect diseased crops

...[S]cientists at the Defense Advanced Research Projects Agency (DARPA) want to capitalize on insects’ natural relationships with plants. They believe ...
White House science advisors urge CRISPR bioterrorist defense strategy

White House science advisors urge CRISPR bioterrorist defense strategy

Scientific advisers to President Obama warn that the U.S. urgently needs a new biodefense strategy and should regularly brief President-elect ...
WHO: GMO cows that produce human antibodies could revolutionize how we fight Ebola, flu

WHO: GMO cows that produce human antibodies could revolutionize how we fight Ebola, flu

SAB Biotherapeutics of South Dakota has genetically engineered cattle to produce large quantities of human antibodies—proteins that help remove harmful ...

Despite hype and promise of cures, only a few gene therapy trials have yielded helpful drugs

Most experts in the medical field will tell you that gene therapy has finally come of age, but the numbers ...

Genome databases, immunotherapy combination may be key in fighting cancer

Immunotherapy is being hailed as the future of cancer treatment. Harnessing the body’s own immune system to attack and kill ...