5-17-2019 phage news

Podcast: CRISPR advances, HIV cures and a perfect predator for superbugs

Exploring the latest advances in medical biotechnology including CRISPR-based gene therapies, infection-fighting viruses and a cure for HIV. Plus reflections ...
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Rejuvenate Bio’s gene therapy shows promise at reversing aging—in mice

Harvard synthetic biology pioneer George Church generated some buzz last year when he co-founded Rejuvenate Bio with the goal of ...
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Animal safety concerns prompt FDA to halt study testing Zolgensma gene therapy for spinal muscular atrophy

The Food and Drug Administration has halted a clinical trial of Novartis’ Zolgensma gene therapy due to a safety concern ...
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Viewpoint: Netflix’s new horror movie ‘Eli’ is a fright. But why did they have to ‘tarnish gene therapy’?

Attempts to treat genetic disease shouldn’t be the stuff of horror films ...
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Gene therapy pioneer James Wilson makes a comeback after disastrous start

Twenty years ago, a young man named Jesse Gelsinger was injected with a large dose of gene-shuttling viruses designed in ...
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A businessman’s daughter has an ‘ultra-rare’ disease, so he immersed himself in science to find a gene therapy cure

Simon and Nina Frost had spared no expense, taking Annabel to all the best neurologists around the country. Finally a ...
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We can identify ‘bad’ genes. Why can’t we use CRISPR gene editing to get rid of them?

Gene therapy 2.0 using CRISPR to knock out harmful genes sounds is a great idea--if and when it works. But ...
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Answering key questions about CRISPR gene therapies

What is gene editing?  Genome editing (also known as gene editing) is a group of technologies that provide scientists with ...
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Application for pricey gene therapy Zolgensma contained manipulated data, but drug will remain on market, FDA says

The Food and Drug Administration said Tuesday [August 7]  that Novartis submitted manipulated data as part of its application for ...
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5 ways we could pay for expensive life-saving gene therapies

We have arrived at a special moment in health care. Innovative, life-changing gene therapies are here that will cure or ...
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How this promising gene therapy for a rare neuromuscular disease was fueled by passionate parents and a dog

The gene therapy will be too late for Joshua Frase. But it will be his legacy ...
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Why we shouldn’t view gene therapy as a treatment of last resort

Providers and payers must ask themselves a two-pronged question about gene therapy: Who should be treated and when? … The ...
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Gene therapy’s fight against ‘bubble boy’ disease may have yielded a safe cure

“Cure” is a strong word, but the authors are confident that it has been achieved ...
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Gene therapy could be revolutionary—if we can figure out how to pay for it

Dozens of revolutionary gene therapies that mend faulty strands of DNA are on their way, bringing the power to eliminate ...
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Gene therapy for beta-thalassemia blood disorder one step closer to European approval

The first gene therapy to treat a rare blood disorder is one step closer to approval [March 29] following a ...
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Why gene therapy’s potential is attracting intense interest from Big Pharma

Big Pharma has been struggling for years to produce drugs that are major breakthroughs in medicine. For these companies, gene ...
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Viewpoint: Call for moratorium on heritable gene editing reminds us of gene therapy’s troubled early days

A group of influential scientists have urged that clinical use of CRISPR be put on hold in the wake of ...
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Inside the quest to use gene therapy to cure a form of congenital blindness

[I]nherited retinal disease affects thousands of people around the world—people who are born with poor vision and then slowly lose ...
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Alzheimer’s disease targeted with gene therapy trial

There’s a test for Alzheimer’s risk that genetic counselors don’t like to talk about. It’s not that they’re hiding the ...
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Gene therapy could offer ‘one-time genetic tune-up’ for Alzheimer’s patients

No one knows for certain what causes Alzheimer’s disease. But one fact about the condition has gained nearly irrefutable status ...
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Rare brain disorder—Angelman syndrome—could be treated with gene therapy in the womb

Scientists are developing a radical form of gene therapy that could cure a devastating medical disorder by mending mutations in the brains ...
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First human test for gene therapy targeting most common cause of blindness

A woman from Oxford has become the first person in the world to have gene therapy to try to halt ...
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Viewpoint: It’s time for a debate on precision medicine and its failed promises

Although some niche applications have been found for precision medicine, and gene therapy is now becoming a reality for a ...
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‘Psychology of extremism’: People most opposed to GMO crops are least informed about science

The people who hold the most extreme views opposing genetically modified (GM) foods think they know most about GM food ...
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Can gene therapy offer a cure for sickle-cell disease?

[I]n November, six months after [21-year-old Manny] Johnson became the first patient to receive an experimental therapy aimed at curing ...
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Inside a couple’s quest to pay for an experimental gene therapy to save their children

“We need your help, we really do,” Gary [Landsman] says, his voice breaking. The Landsmans’ two sons—Benny, then 18 months, ...
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Why the patent system could help shape the future of gene editing

A crucial part of the arsenal for shaping the future of gene editing is hiding in plain sight: the patent ...
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Can we afford gene therapy’s million-dollar price tags?

[4-year-old] Caspian was born with a rare, inherited eye disorder called Leber congenital amaurosis, which results in the progressive deterioration ...
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