hemophilia
Hemophilia B—the blood disease that plagued Europe’s royal families—might be treatable using gene editing
Researchers are hoping to use gene editing to create more effective and less expensive treatment options--compared to gene therapy--for people ...
Living with hemophilia: When patients with genetic disorders don’t want to be cured
Jeff Johnson is 40 years old, and for all 40 of those years, he has been living with hemophilia. The ...
Bringing us closer to ‘once-in-a-lifetime’ hemophilia treatment with experimental gene therapies
Scientists are edging closer to defeating a longtime enemy of human health: hemophilia, the inability to form blood clots. After ...
Gene therapy on brink of golden age: Here’s why
Just as vaccination began first for smallpox, then expanded to a handful of other diseases and has since expanded to ...