2-19-2019 angelman clinic feature

Rare brain disorder—Angelman syndrome—could be treated with gene therapy in the womb

Scientists are developing a radical form of gene therapy that could cure a devastating medical disorder by mending mutations in the brains ...
Gene therapy for autism? Rare Angelman syndrome could answer key questions

Gene therapy for autism? Rare Angelman syndrome could answer key questions

[T]he success of genetic therapies [for autism] is not guaranteed. Even if disrupted genes can be replaced, repaired or otherwise ...