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Can we afford gene therapy’s million-dollar price tags?

[4-year-old] Caspian was born with a rare, inherited eye disorder called Leber congenital amaurosis, which results in the progressive deterioration ...
blindness

Pioneering gene therapy restores vision to people with rare retinal blindness

Spark Therapeutics is moving forward with its treatment for a type of inherited retinal dystrophy. In the wake of the ...