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CRISPR provides ‘functional cure’ for patients with beta thalassemia, sickle cell disease, preliminary study shows

Result of this ongoing trial, which is the first to use CRISPR to treat inherited genetic disorders, were announced [June ...
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Bluebird Bio defends as ‘simple and human’ its pricing of costly gene therapy for beta thalassemia

[J]ust as we spent the past years cracking the code to make gene therapy work, we now need to work ...
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‘First ever’ human CRISPR trial targets rare beta thalassemia blood disorder

CRISPR, the groundbreaking and controversial gene-editing technique, has been used in a patient with a debilitating blood disease, scientists revealed ...