patient image

CRISPR provides ‘functional cure’ for patients with beta thalassemia, sickle cell disease, preliminary study shows

Result of this ongoing trial, which is the first to use CRISPR to treat inherited genetic disorders, were announced [June ...
sickle

Can gene therapy offer a cure for sickle-cell disease?

[I]n November, six months after [21-year-old Manny] Johnson became the first patient to receive an experimental therapy aimed at curing ...
gene editing

CRISPR-Cas9 is hot but it’s not the only way to edit a genome

Despite its growing track record and huge potential, CRISPR-Cas9 genome editing may not be the magic bullet for all applications ...