sickle cell disease
CRISPR provides ‘functional cure’ for patients with beta thalassemia, sickle cell disease, preliminary study shows
Result of this ongoing trial, which is the first to use CRISPR to treat inherited genetic disorders, were announced [June ...
Can gene therapy offer a cure for sickle-cell disease?
[I]n November, six months after [21-year-old Manny] Johnson became the first patient to receive an experimental therapy aimed at curing ...
CRISPR-Cas9 is hot but it’s not the only way to edit a genome
Despite its growing track record and huge potential, CRISPR-Cas9 genome editing may not be the magic bullet for all applications ...