Emily Mullin
Beta thalassemia patients could be freed from life of blood transfusions by one-time gene therapy
A one-time, experimental treatment for an inherited blood disorder has shown dramatic results in a small study. It’s a major ...
Viewpoint: We need to know if CRISPR works in monkeys and possible off-target effects before we start human trials
Sometime this year, people in the US and Europe will start getting treated for diseases using the gene-editing tool CRISPR, but ...
Building an Alzheimer’s early warning system through artificial intelligence
[A flat white box attached to the wall] knows when [David Graham] gets out of bed, gets dressed, walks to ...
Saving critically ill babies through lightning-fast genome sequencing
Usually it takes weeks for scientists to sequence an entire genome. But [neurologist Jennifer] Friedman and her colleagues at Rady [Children’s ...
Huntington’s patients find new hope in ‘gene-silencing’ drug
Huntington’s is a genetic disorder that causes nerve cells in the brain to gradually break down, leading to irreversible brain ...
8 common cancers could be detected early with $500 blood test
A simple-to-take test that tells if you have a tumor lurking, and even where it is in your body, is ...
CRISPR first in US: Human cancer patients to be treated with gene-editing tool
The first human test in the U.S. involving the gene-editing tool CRISPR could begin at any time and will employ ...
Rural-urban divide: Groundbreaking gene therapies could exacerbate inequality in cancer care
Two new cancer treatments have shown miraculous cures, but if you happen to live in Arkansas or Montana, or a ...
Why 2018 might not be a banner year for CRISPR gene editing in humans
Ever since scientists first used CRISPR-Cas9 to edit living human cells in 2013, they’ve been saying that the possibilities for ...
Why life-saving gene therapy isn’t available yet to children who need it most
[The first patient to permanently edit his DNA,] Brian Madeux, 44, of Arizona, is part of a clinical trial testing ...
How gene therapy could help fight methamphetamine addiction
Gene therapy, which modifies a person’s DNA, has long been thought of as a way to treat genetic diseases—and, more recently, ...
Talking Biotech: Pet dogs with genetic diseases testing ground for gene therapy
Journalist Emily Mullin: Gene therapies becoming more promising but restricted in humans because of safety concerns, prompting some researchers to ...
Inserting CRISPR machinery into human cells to fight Huntington’s and Lou Gehrig’s
The gene-editing tool CRISPR is based on a natural defense system embedded in bacterial cells that recognizes and destroys invading ...
Edible ‘CRISPR pill’ could make harmful bacteria self-destruct
As resistance to antibiotics grows in the U.S., researchers are looking for new ways to fight germs like Clostridium difficile, a ...
$500K gene therapy treatment? Some see a bargain
The idea behind gene therapy is that genetic material is used as a “living drug” to treat disease. Scientists have been ...
5 companies leading the personal genomics revolution
As gene sequencing technology gets faster and cheaper, companies are finding more ways to commercialize DNA, from offering disease-specific genetic ...
What’s next in consumer genetics? Helix’s ‘app store for your genome’
A Silicon Valley startup called Helix is betting on the notion that not only do people want to learn more ...
Darwin Life: ‘Three-parent babies’ as a cure for age-related infertility
John Zhang, a U.S. fertility doctor has started a company [called Darwin Life] with a provocative vision for older women: become ...
Physicians missing cancer diagnoses by not ordering gene tests
A small company called Loxo Oncology thinks it can treat every cancer patient that harbors a specific, unusual, genetic mutation...The ...
Keytruda drug treats cancer based on tumor’s genetics rather than its location
In a first for precision medicine, a cancer drug has won regulatory approval based on the genetic characteristic of tumors, ...
Bubble boy hope: Strimvelis gene therapy revises genetic make-up, offers rare immune deficiency cure
A child in Europe has become the second individual ever to receive a commercial gene therapy, according to GlaxoSmithKline. The ...
Edible ‘CRISPR pill’ instructs harmful bacteria to self-destruct, may revolutionize fight against antibiotic resistance
As resistance to antibiotics grows in the U.S., researchers are looking for new ways to fight germs like Clostridium difficile, ...
No longer waiting idly: Parents of patients establishing gene therapy programs
In recent years, gene therapies have become safer and better at hitting their intended targets in the body, leading to ...
5 biotech products US regulators might struggle to regulate
A new report issued by the National Academy of Sciences says U.S. regulatory agencies need to prepare for new plants, ...
‘Speeding up evolution’: Artificial yeast project could boost drug, biofuel production
An international team of scientists is closing in on its goal of replacing all the genetic material in a yeast ...
Brain cancer in children: Unique ‘genetic drivers’ open door to precision medical treatments
In the past 30 years, childhood deaths from cancer have declined by 50 percent overall, but those from pediatric brain ...
Our voices and smartphones may soon help diagnose diseases and stress disorders
Voice samples are a rich source of information about a person’s health, and researchers think subtle vocal cues may indicate ...
Personalized cancer vaccines could revolutionize treatment and prevent relapse
Ernest Levy joined an early-stage clinical trial led by the Beth Israel Deaconess Medical Center, testing a cancer vaccine for ...
