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Podcast: Gene therapy could be best hope to cure Duchenne muscular dystrophy

Conner Curran was 4 when he was diagnosed with Duchenne muscular dystrophy. His muscles were already beginning to waste away ...
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Patient’s ‘serious’ kidney injury halts gene therapy trial for Duchenne muscular dystrophy

The Food and Drug Administration has halted a clinical trial involving a Duchenne muscular dystrophy gene therapy from Solid Biosciences ...
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Why gene editing isn’t ready for treating human disease: It’s not ‘efficient enough’

Gene editing will likely always come with a bit of risk; when you're cutting and pasting DNA in millions of ...
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Why ending muscle wasting matters for curing cancer

Deterioration of muscle is the cause of death in many diseases, like cancer, but no treatments address this lethal symptom ...
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Promising treatment for Duchenne muscular dystrophy developed with CRISPR gene editing

Duchenne muscular dystrophy is a life-threatening muscle-wasting illness. Occurring mostly in males, it is the most common type of muscular ...
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CRISPR treatment for dogs with muscular dystrophy could one day lead to a cure for humans

Dogs suffering from muscular dystrophy are having their genomes edited with CRISPR, and the results are “mind-blowing.” Researchers from Texas ...
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Duchenne muscular dystrophy gene therapy trial put on hold

Sarepta Therapeutics’ clinical trial for a gene therapy to treat Duchenne muscular dystrophy has been paused by the Food and ...
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Human muscles from stem cells: Advance could aid research into muscular dystrophy, other diseases

Muscle created with stem cells is not quite as strong as the researchers would like. But they think these new ...
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Gene therapy 2.0: Will CRISPR make expensive treatment accessible to all?

Gene therapy, at a million dollars a treatment, will run up a patient's medical bill quickly. Can CRISPR-Cas9 gene editing ...