The following is an excerpt.
A single session of a gene therapy developed by the Universitat Autònoma de Barcelona (UAB) cures Sanfilippo Syndrome A in animal models. This syndrome is a neurodegenerative disease that affects between 1 and 9 out of every 100,000 children, and causes the death of the child on reaching adolescence.
Read the full story here: Gene Therapy Cures a Severe Pediatric Neurodegenerative Disease in Animal Models