Can CRISPR really save lives? People with beta thalassemia blood disease likely first human trial subjects

| | December 15, 2017
crispr dna editing x
This article or excerpt is included in the GLP’s daily curated selection of ideologically diverse news, opinion and analysis of biotechnology innovation.

For those who have no idea what CRISPR is all about, the abbreviation means “Clustered Regularly Interspaced Short Palindromic Repeats.” It’s a family of DNA sequences in bacteria. The sequences here play a huge role in fighting bacteria within the body, and if improved, could fight dangerous illnesses as well. This technology for gene-editing treatment has been in the works for quite some time, but could finally come to market due to a company known as CRISPR Therapeutics.

The company says it’s ready to test its findings on people, and as such, it has asked regulators in Europe to allow them the chance to cure the disease, beta thalassemia. The plan is to add genetic corrections to the blood cells of the affected. Should everything go according to plan, the study could begin as soon as 2018.

[T]hree companies came on the scene with the task of changing the health sector forever. These companies are CRISPR Therapeutics, Editas Medicine and Intellia Therapeutics. All are located at MIT in Cambridge, Massachusetts, and just a few blocks from each other.

When these startups first came on the scene, much of what was needed were left up to the imagination of investors. Still, they have managed to move quite quickly to get CRISPR from the testing stage to a point where it’s ready for human testing.

CRISPR

Read full, original post: Biotech Companies Are Preparing the First CRISPR Test on Humans

Outbreak
Outbreak Daily Digest
Biotech Facts & Fallacies
Talking Biotech
Genetics Unzipped
sperm swim

Video: Sperm are ‘spinners not swimmers’—because they are lopsided

Research by fertility scientists in the UK and Mexico challenges the accepted view of how sperm “swim”, suggesting that it ...
mag insects image superjumbo v

Disaster interrupted: Which farming system better preserves insect populations: Organic or conventional?

A three-year run of fragmentary Armageddon-like studies had primed the journalism pumps and settled the media framing about the future ...
dead bee desolate city

Are we facing an ‘Insect Apocalypse’ caused by ‘intensive, industrial’ farming and agricultural chemicals? The media say yes; Science says ‘no’

The media call it the “Insect Apocalypse”. In the past three years, the phrase has become an accepted truth of ...
breastfeeding bed x facebook x

Infographic: We know breastfeeding helps children. Now we know it helps mothers too

When a woman becomes pregnant, her risk of type 2 diabetes increases for the rest of her life, perhaps because ...
biotechnology worker x

Can GMOs rescue threatened plants and crops?

Some scientists and ecologists argue that humans are in the midst of an "extinction crisis" — the sixth wave of ...
food globe x

Are GMOs necessary to feed the world?

Experts estimate that agricultural production needs to roughly double in the coming decades. How can that be achieved? ...
eating gmo corn on the cob x

Are GMOs safe?

In 2015, 15 scientists and activists issued a statement, "No Scientific consensus on GMO safety," in the journal Environmental Sciences ...
Screen Shot at PM

Charles Benbrook: Agricultural economist and consultant for the organic industry and anti-biotechnology advocacy groups

Independent scientists rip Benbrook's co-authored commentary in New England Journal calling for reassessment of dangers of all GMO crops and herbicides ...
Screen Shot at PM

ETC Group: ‘Extreme’ biotechnology critic campaigns against synthetic biology and other forms of ‘extreme genetic engineering’

The ETC Group is an international environmental non-governmental organization (NGO) based in Canada whose stated purpose is to monitor "the impact of emerging technologies and ...
Share via
News on human & agricultural genetics and biotechnology delivered to your inbox.
Optional. Mail on special occasions.
Send this to a friend