A new class of medicines could give doctors the ability to awaken underperforming genes in patients who currently have no treatment options.
Boston-area startup RaNA Therapeutics is developing a novel kind of medicine that can boost the activity of genes that may be silenced or underactive and thus cause disease. The medicine would use a small RNA-like molecule that blocks the function of a long RNA molecule that is hampering the expression of such a gene.
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Read the full, original story here: RNA Drugs Target Genes That Were Once Off-Limits
