do organic wines age

Podcast: ‘Clean’ wine isn’t so clean; FDA blocks hemophilia gene therapy; Universal flu vaccine?

Actress Cameron Diaz and fashion entrepreneur Katherine Power are marketing a new brand of "clean" wine using long-debunked claims about ...
closeup of doctors hand holding ct brainscan

Strokes often deadly but gene therapy offers hope to rebuild critically damaged brain cells

When you think of a typical meal in the US South, you will likely recall the rich, hearty dishes that ...
baby lucy

Lucy may not live to see her second birthday without expensive gene therapy

Lucy Van Doormaal was born on April 1 in Vancouver, but before her parents, Scott and Laura Van Doormaal, could ...
eye

Podcast: Let the light shine—Tackling eye disease with gene therapy

Researchers are bringing discoveries about the underlying genetic faults that cause eye diseases all the way through to game-changing gene ...
batten hope featured img

Another COVID-19 casualty: ‘Major delays’ for gene therapy trials for rare diseases

While the ongoing COVID-19 pandemic won’t have much of an impact on cash available for new biotech startups, it has ...
colorblind

Gene therapy could restore color vision for people who see the world in shades of gray

In a small trial in Germany, an experimental gene therapy improved the vision of nine people with total color blindness, ...
yk oav a jfrdocevhmn wdwfi

Ultimate fitness hack: Imagine being able to build muscles with a gene therapy

Trying to hack fitness is a multi-million-dollar industry; we’ve all seen at least one ad featuring a purported miracle product ...
gene

What’s holding up gene therapy? Making drugs on a large scale

As interest in gene therapy grows, manufacturers face physical, biological, and engineering challenges to developing and producing drugs on a ...
gerstenkorn aufstechen

Common form of inherited blindness shows ‘massive improvements’ with experimental gene therapy

This month, K.L. became one of the first patients to receive a new experimental gene therapy for children with a ...
obesity mn edccc d bffbd c ab f b fit w

Gene therapy shows success against some cancers and inherited disorders. Can it tackle obesity?

Scientists are working with treatments that have shown success in amping up the metabolism of mice, helping them lose weight ...
bearwalk broad gaddy

900 gene therapy drugs are in the pipeline. How does the FDA want to regulate them?

To date, the FDA has approved four gene therapy products, which insert new genetic material into a patient’s cells. The ...
unnamed file

Gene therapy for Alzheimer’s? Biotech startup suggests new approach, using dementia ‘off switch’

What if there were a single mechanism in the brain that, when faulty, leads to all kinds of dementias? And ...
theweekly myblood promo videosixteenbynine v

Teenager’s experimental gene therapy treatment could change the lives of millions of sickle cell patients worldwide

Meet Helen Obando, a shy 16-year-old who likes to dance when her body isn’t ravaged by the debilitating symptoms of ...
luxturna x

Gene therapy era: A look at current treatments and what’s next for cancers and genetic disorders

At least nine gene therapies have been approved for certain kinds of cancer, some viral infections and a few inherited ...
ke eckghiii rkm b r bofuui

Gene therapy offers hope for untreatable CTE brain disorder

[Researchers from Weill Cornell Medical College] published a new study (“Anti-Phospho-Tau Gene Therapy for Chronic Traumatic Encephalopathy”) in Human Gene Therapy that ...
merlin b d bebf e a d d a articlelarge

Virus used to deliver gene therapy treatments may increase liver cancer risk, study suggests

Just as gene therapy finally seems to be living up to its promise, a study has revived a lingering worry ...
xenotransplantation

Forecasting: 2020 could bring major advances in gene therapies and pig-to-human organ transplants

Here are two stories in biotech we’re keeping our eyes on. Although successes likely won’t come to fruition this year ...
shutterstock x @ x

Will 2020 see the debut of promising gene therapy for hemophilia A? It’s up to the FDA.

Hemophilia A gene therapy has been twenty years in the making ...
the gene therapy market is going to produce a microsoft

2019 offered ‘eclectic’ mix of potentially breakthrough treatments for genetic diseases, from cystic fibrosis to sickle cell

2019 was a very good year for new treatments of genetic diseases ...
cas virus v custom efeafcabfa cbe cd e b d c ca dd b s c

‘CRISPR this, CRISPR that’: Is our fascination with the popular gene-editing tool distracting us from the potential of gene-silencing RNAi technology?

I hope the public fascination with CRISPR can also embrace the other biotechnologies providing new therapeutic options ...
bb a o

Would price controls hamper research on gene therapy and other innovative treatments?

Over the next decade, it is a near certainty that we will have gene-therapy cures for deadly inherited disorders such ...
anti aging drugs senolytics

$1 million for anti-aging gene therapy? ‘Dubious’ treatment raises ethical concerns

Would you pay $1 million and fly to South America for a chance to live longer? Libella Gene Therapeutics, a ...
nn kda worlds most expensive drug x

Viewpoint: Spinal muscular atrophy treatment Zolgensma a gene therapy trailblazer, despite controversy

In August, the US Food and Drug Administration (FDA) gave drug manufacturer AveXis, Inc, a subsidiary of Novartis AG, a ...
im

Viewpoint: Experimental gene therapy saved my sons’ eyesight

Not long after we brought my newborn son, Anthony, home from the hospital, we noticed his eyes kept darting to ...
stat bluebird x

Bluebird Bio defends as ‘simple and human’ its pricing of costly gene therapy for beta thalassemia

[J]ust as we spent the past years cracking the code to make gene therapy work, we now need to work ...
retro boyinthebubble superjumbo

Gene therapy may offer cure for debilitating ‘bubble boy disease’

Omarion was born with a rare genetic disorder called X-linked severe combined immunodeficiency (SCID), better known as the “bubble boy ...
ht shirley donald keena jef x

Trio of gene therapies seeks to reverse age-related diseases to make us ‘healthy, youthful later in life’

The legendary synthetic biologist Dr. George Church and team at the Wyss Institute at Harvard University took a first step towards ...
maxresdefault

Patient’s ‘serious’ kidney injury halts gene therapy trial for Duchenne muscular dystrophy

The Food and Drug Administration has halted a clinical trial involving a Duchenne muscular dystrophy gene therapy from Solid Biosciences ...
Loading...